LA-based Renovaro Biosciences develops advanced cell and gene therapies for cancer and infectious diseases.
Sarepta Therapeutics, a US-based biopharmaceutical firm, specializes in medical research and drug development.
Nephrogen: Crafting gene cures for kidney diseases, focusing on PKD.
Epic Bio: Pioneering the new era of gene expression modulation.
Kriya Therapeutics: Pioneering gene therapies for global health challenges in ophthalmology, neurology, and metabolism.
Ligandal: Pioneering personalized genetic medicine through nanotechnology.
Locana: Pioneering RNA-targeting gene therapies for devastating diseases.
Affinia Therapeutics: A biotech firm innovating gene therapies for muscle and CNS diseases.
Opsin Biotherapeutics: Pioneering opsin-based gene therapies for effective pain management.
US-based Precigen, Inc. develops global gene and cell therapies for immuno-oncology, autoimmune disorders, and infections.
Carmine Therapeutics: Pioneering non-viral gene therapies via red blood cell vesicles.
ExcepGen: A San Francisco-based biotech firm innovating in drug discovery for next-gen therapeutics.
Castle Creek Biosciences: Personalized gene therapies for rare skin and connective tissue disorders.
Taysha Gene Therapies: Developing curative medicines to eradicate severe CNS diseases.
Excision BioTherapeutics: A San Francisco-based biotech firm developing gene therapies for HIV.
San Diego-based Poseida Therapeutics, Inc. is a clinical-stage biopharmaceutical company innovating cell and gene therapeutics.
Excellos: Pioneering developer and manufacturer of cell and gene therapies.
Bluebird Bio, Inc.: A US-based biotech firm offering gene therapies for severe genetic disorders.
Twister Biotech: Advancing gene therapies for rare cancers and autoimmune diseases through innovative MiniVectors.
Prevail Therapeutics: A NY-based biotech firm developing gene therapies for neurodegenerative disorders.
Basecamp Bio: Pioneering cell, gene therapies, regenerative medicine, and immunotherapies research.