
PTC Therapeutics, Inc.: A US-based pharmaceutical company specializing in oral, small-molecule drugs for genetic disorders, oncology, and infectious diseases.
ptcbio.comCrawled Oct 15, 2026
PTC says it is committed to children and adults living with rare diseases who have few or no treatment options, and that its culture reflects this mission.
The company aims to provide treatment for pediatric and adult patients with rare diseases for which few or no treatment options are available.
PTC offers benefit options to employees globally to address their diverse needs.
PTC says changing the course of rare diseases is its purpose and describes its culture as supporting employees’ ability to bring their whole authentic selves to work.
Anne has over a decade of experience partnering with patients, caregivers, and cross-functional teams to bring patient perspectives into drug development, clinical trials, and commercialization. She leads patient engagement strategy across neurology and pipeline programs.
Emily is a Patient Engagement Liaison at PTC Therapeutics. She holds bachelor’s and master’s degrees from Florida State University and Illinois State University and studied Child Life, advocating for children and families during hospital experiences.
Frank leads patient engagement efforts in North America. His team focuses on Duchenne muscular dystrophy (DMD), phenylketonuria (PKU), Friedreich ataxia (FA), and aromatic L-amino acid decarboxylase (AADC) deficiency, providing education and resources to help families advocate for themselves.
Karina serves as a Patient Engagement Liaison on the North America team. Before joining, she spent nearly a decade at the Muscular Dystrophy Association (MDA), leading fundraising and educational initiatives, including directing MDA Summer Camp.
PTC Therapeutics K.K. was established on June 24, 2015. Stefan Sakurai is its president and representative director, and its address is 4-12-20 Nihonbashi-Honcho, Chuo-ku, Tokyo 103-0023.
The page says personal information provided when contacting the company is handled in accordance with its Privacy Statement.
The company has a global network.
The page lists the Dublin headquarters and contact details for PTC Therapeutics International Limited, and the corporate headquarters of PTC Therapeutics, Inc. at 500 Warren Corporate Center Drive, Warren, NJ 07059.
The page lists the Guildford address and contact details for PTC Therapeutics Limited, and identifies PTC Therapeutics, Inc. as the corporate headquarters.
PTC Therapeutics develops treatments for rare diseases.