
Discovering RNAi therapeutics for genetic diseases. Founded in 2002, headquartered in Cambridge, MA.
Founded in 2002 and headquartered in Cambridge, Massachusetts, Alnylam Pharmaceuticals is a pioneering biopharmaceutical company dedicated to discovering, developing, and commercializing novel therapeutics based on ribonucleic acid interference (RNAi). The company's mission is to harness RNAi to silence the genes that cause human diseases, offering innovative treatments for genetic conditions, cardio-metabolic diseases, hepatic infectious diseases, and central nervous system (CNS)/ocular diseases. Alnylam’s marketed products include ONPATTRO (patisiran), a lipid complex injection for treating the polyneuropathy of hereditary transthyretin-mediated amyloidosis.
Notable figures affiliated with Alnylam include its co-founder and Nobel laureate Phillip Sharp. The company has attracted significant investment from leading venture capital firms and strategic partners. Key achievements include the successful commercialization of multiple RNAi-based therapies and a robust pipeline addressing a broad range of diseases. Alnylam's impact extends beyond rare diseases, aiming to improve the lives of millions through its groundbreaking RNAi technology.

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Companies similar to Alnylam Pharmaceuticals aln include Ionis Pharmaceuticals, Sirnaomics, Silence Therapeutics and Atalanta Therapeutics.
Alnylam Pharmaceuticals aln was founded in 2002.
Alnylam Pharmaceuticals aln's headquarters is located in Cambridge, MA, US.
Alnylam Pharmaceuticals aln's most recent funding round was for $900M (USD) in September 2022.
As of Sep 13, 2022, Alnylam Pharmaceuticals aln has raised a total of $3.9B (USD).
Alnylam Pharmaceuticals aln has 2,002 employees as of Feb 6, 2024.