Regulus Therapeutics Inc., founded in September 2007 by Alnylam Pharmaceuticals and Isis Pharmaceuticals, is a clinical-stage biopharmaceutical company based in San Diego, California. The company's core mission is to develop first-in-class drugs that target microRNAs to treat a broad range of diseases, with a particular focus on orphan kidney diseases such as Autosomal Dominant Polycystic Kidney Disease (ADPKD). Regulus leverages its expertise in microRNA-based therapeutics to address high unmet medical needs, aiming to improve the lives of patients and their families.
Notable affiliated individuals include founders from Alnylam Pharmaceuticals and Isis Pharmaceuticals. Regulus has garnered attention for its innovative approach and has achieved significant milestones, including positive topline data from clinical trials. The company's pioneering work in microRNA therapeutics has positioned it as a leader in the biopharmaceutical industry, making a substantial impact on the treatment landscape for kidney diseases.