AMX0114 is an investigational antisense oligonucleotide targeting calpain-2 in early development for ALS.

Amylyx Pharmaceuticals: A global biopharmaceutical firm innovating therapies for ALS and neurodegenerative diseases.
Amylyx Pharmaceuticals, founded with a mission to discover and develop treatments for neurodegenerative diseases, focuses primarily on amyotrophic lateral sclerosis (ALS) and other similar conditions. The company offers proprietary therapeutic solutions aimed at improving the quality of life for individuals affected by these relentless diseases. Amylyx serves a global market, dedicated to creating more meaningful moments for patients and their families.
Notable figures associated with Amylyx include its founders and key investors who have supported its innovative approach to biopharmaceutical development. The company has achieved significant milestones, including the development of promising therapies that have shown potential in clinical trials. Amylyx's impact is marked by its commitment to the neurodegenerative disease community, striving to bring hope and improved outcomes to those living with these challenging conditions.
Companies similar to Amylyx Pharmaceuticals include Leal Therapeutics, Shionogi & Co., Sanofi and Biogen.
Amylyx Pharmaceuticals was founded in 2014.
Amylyx Pharmaceuticals' headquarters is located in Cambridge, MA, US.
Amylyx Pharmaceuticals' most recent funding round was for $246.3M (USD) in October 2022.
As of Oct 6, 2022, Amylyx Pharmaceuticals has disclosed funding of $448.5M (USD). Undisclosed round amounts are excluded.
Amylyx Pharmaceuticals has 262 employees as of Feb 6, 2024.
AMX0035 is an investigational oral combination of sodium phenylbutyrate and taurursodiol in development for Wolfram syndrome.
biogen.com